Gene therapy (transfer or addition)
research in hemophilia is rapidly evolving every day. While more information will become available over
time, the following questions may help you better understand today’s knowledge around gene therapy for
hemophilia.
Gene therapy (transfer or addition)
The transfer or addition of genetic material into a cell. Once in the cell, a
working copy of a gene can help make proteins despite the presence of a faulty or mutated gene.
Download a summary about the potential of gene therapy research in hemophilia.
Download Brochure
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